International Registry Study of Neutral Lipid Storage Disease (NLSD) / Triglyceride Deposit Cardiomyovasculopathy (TGCV) and Related Diseases
Recruiting
Observational Study
Neutral Lipid Storage Disease
No Placebo Group
Every participant receives an active treatment — no one gets a placebo.
No Study Drug
Researchers observe your health over time — no experimental treatment is given.
At a Glance
- Sex
- Any
- Study type
- Observational
- Participants needed
- 120 (estimated)
- Sponsor
- Translational Research Center for Medical Innovation, Kobe, Hyogo, Japan · Other
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About This Trial
This study aims to understand the state of onset of NLSD(neutral lipid storage disease) / TGCV(triglyceride deposit cardiovasculopathy) worldwide, background information of affected patients, and natural history of the disease, as well as exploring the prognostic factors and assessing the efficacy of disease-specific treatment.
Trial Locations
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Eligibility Criteria
Inclusion Criteria:
* Patients who are diagnosed with NLSD / TGCV
Exclusion Criteria:
* None
Contacts
Kenichi Hirano, MD, Ph.D
+81-6-6872-8215
CONTACT