A Multicenter Multinational Observational Study of Children With Hypochondroplasia
Recruiting
Observational Study
Hypochondroplasia
No Placebo Group
Every participant receives an active treatment — no one gets a placebo.
No Study Drug
Researchers observe your health over time — no experimental treatment is given.
At a Glance
- Age
- Up to 15
- Sex
- Any
- Study type
- Observational
- Participants needed
- 400 (estimated)
- Sponsor
- BioMarin Pharmaceutical · Industry
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About This Trial
This study will assess growth over time and the clinical course of HCH in children by collecting growth measurements and other variables of interest.
Trial Locations
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Eligibility Criteria
Inclusion Criteria:
* Participants must be ≤ 15 years old at the time of signing the informed consent
* Participants must have genetic confirmation of Hypochondroplasia diagnosis
Exclusion Criteria:
* Have a diagnosis of another genetic short stature condition other than Hypochondroplasia or a ge…
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