FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases

Recruiting Observational Study
Alpha-Thalassemia Beta-Thalassemia Amyloidosis Amyotrophic Lateral Sclerosis Creutzfeld-Jakob Disease Cystic Fibrosis Duchenne Muscular Dystrophy Early-Onset Alzheimer Disease Ehlers-Danlos Syndrome Huntington Disease Gaucher Disease GM1 Gangliosidosis Myasthenia Gravis Pompe Disease Sickle Cell Disease Transthyretin Amyloid Cardiomyopathy Rare Diseases
No Study Drug Researchers observe your health over time — no experimental treatment is given.
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At a Glance
Sex
Any
Study type
Observational
Participants needed
1,000 (estimated)
Sponsor
xCures · Industry
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About This Trial
FLOWER is a completely virtual, nationwide, real-world observational study to collect, annotate, standardize, and report clinical data for rare diseases. Patients participate in the study by electronic consent (eConsent) and sign a medical records release to permit data collection. Medical records are accessed from institutions directly via eFax or paper fax, online from patient electronic medical…
Trial Locations
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Eligibility Criteria
Inclusion Criteria: * Any person with a known or suspected rare disease, defined by their prevalence of fewer than 200,000 individuals nationwide. Diseases include but are not limited to: Alpha- or Beta- Thalassemia Amyloidosis Amyotrophic Lateral Sclerosis (ALS) Creutzfeldt-Jakob disease (CJD) Cy…
Contacts

Mark Shapiro, MS

707-641-4475

expandedaccess@xcures.com

CONTACT