Investigating Phenotypic, Epigenetic, and NeuroGenetic Traits in Rare and Ultra-rare Neurodevelopmental Disorders (Project PENGUIN)

Recruiting Observational Study
Baker Gordon Syndrome Rare Neurodevelopmental Conditions Rare Neurogenetic Conditions Syt-1 Disorder Epilepsy Seizure Genetic Mutations Autism in Children Developmental Delay (Disorder)
Healthy Volunteers Welcome You do not need to have the condition being studied to take part. No Study Drug Researchers observe your health over time — no experimental treatment is given.
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Review the details below, then apply to join this clinical trial.

At a Glance
Age
Up to 99
Sex
Any
Study type
Observational
Participants needed
100 (estimated)
Sponsor
University of Missouri-Columbia · Other
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About This Trial
Rare genetic neurodevelopmental disorders, such as Syt-1 or Baker Gordon Syndrome (BAGOS) arise from mutations in genes essential for brain development and function, often disrupting neurotransmission and neuronal connectivity. These conditions present with a wide range of symptoms including developmental delays, seizures, motor and behavioral challenges, and vary widely in severity. These disorde…
Trial Locations
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Eligibility Criteria
For those with a rare condition: Inclusion Criteria: * Diagnosed or suspected neurogenetic disorder * Individuals 0-99 Exclusion Criteria: * Individuals unwilling or unable to complete visits with the study team. For control parents/caregivers of those with a rare condition: Inclusion Criteria…
Contacts

Sophia R Marchetti

573-882-6720

sophiamarchetti@health.missouri.edu

CONTACT